1214 In Vitro Trans Splicing Mediated CD40 Ligand Gene Therapy for X Linked Immunodeficiency Molecular Therapy Vol 5, No 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy[.]
!" C -!'/% " ?' @ (. " ##D. 3 ?'* ?'*' $*' % !' C( " " C( 1 C( ) !' C( 8 $ 1212 Sustained Gene Expression from Theracyte Immunoisolation Devices Ofer Yanay,1 Lisa Y Flint,1 Margaret Brzezinski,1 Simon C Barry,1 Randall W Barton,2 William R Osborne.1 Pediatrics, University of Washington, Seattle, WA, United States; Gene Therapy/Genomics, Boehringer Ingelheim Pharmaceuticals Inc., Ridgefield, CT, United States ' ->!)/ -"(?/ " $ >!) "(? G 3 @ >!)$*'-D >(*/ "(? $*' -D (*/ D @ (.69 C D ? >!) ? -?/ 0 -0/ C D "(? ? 3 89B , ? >!) -0"0I ?"?/ -0"?I ?"0/ -"0/ "(? -?"?/ >!) "(? 3 8, G@ -0"0I?"?/ -0"?I ?"0/ D >(*" &9H";5H 8, ? C D = C -6&H/ 3 C ,"= ' >!) 8, ' 3 H C -O9998/ 2 >!) @ 3 "(? -O99&/ 3 S394 1213 Delivery of Naked DNA to Skeletal Muscle: Gene Therapy for Severe Anemia David L Lewis,1 Hans H Herweijer,1 Jon Wolff.1 Mirus Corporation, Madison, WI, United States 1 ( - / E ->!)/ ( 3 >!) >!) 3 + >!) ' E $*' 3 >!) 3 G $*' 1214 In V rans-Splicing-Mediated CD40-Ligand Vitro Trans-Splicing-Mediated itro T Gene Therapy for X-Linked Immunodeficiency Minoru Tahara,1 Neil R Hackett,1 Robert G Pergolizzi,1 Jiang Qinshi,1 Ronald G Crystal.1 Weill Medical College of Cornell University, New York, NY, United States F" # G ( 3 , & $69 -$69D/ 3 @ " $69D " -2 * # 855:I 67 8,&=/ - / " 3 $69D $69D 3 $69D " "@*' " @*' $69D " 3 8 "@*' $69D - 3 ,"&/ 3 3 ,"& "@*' " ' $69D 3 8 8 3 ,"6 C' #. ' (.69 ( " 3 ,"& @*' =′ 8 " " C D @ " !@ " ' @ "!@ 3 " " " " " 878 3 1 @ 1 " " @*' " " " " &9 8B= =8, =′ 8 " " " " 1 3 " $69D F" # Molecular Therapy Vol 5, No 5, May 2002, Part of Parts Copyright © The American Society of Gene Therapy !" " $ 1 # " -*'($'S 7 *./ ( @ ' ' 8 855: 4 / # 58 $=6J 0!@> 3 *?" 3 C( AD(?-AJ (8J D" ?=D"/ 58"?! $88"?! C( ?! 3 ? ?! $*' 583 C( 583 "%" -2B"/ @ 2B" G *'$!C 3 -*2 $C@ / - / ) $ 1217 Amelioration of Murine β-thalassemia Following Stem Cell Gene T ransfer with a Human γ-Globin Lentiviral Transfer Vector Derek A Persons,1 Phillip W Hargrove,1 Esther R Allay,1 Hideki Hanawa,1 Arthur W Nienhuis.1 Division of Experimental Hematology, St Jude Children′s Research Hospital, Memphis, TN, United States ) C? β" -! 2 5;7=,;& ,998/ -($/-2 *# B78;;,999 ? 2 5;7689 ,998/ γ" γ" ($ " β9" β" γ" 8; 1 6 = , β" 1 β" -8;5 / ' γ" S395 ... William R Osborne.1 Pediatrics, University of Washington, Seattle, WA, United States; Gene Therapy/ Genomics, Boehringer Ingelheim Pharmaceuticals Inc., Ridgefield, CT, United States '' ... 1212 Sustained Gene Expression from Theracyte Immunoisolation Devices Ofer Yanay,1 Lisa Y Flint,1 Margaret Brzezinski,1 Simon C Barry,1 Randall W Barton,2 William