1068 Correction of the Hematopoietic Phenotype of Fanconi Anemia A Knockout Mice Using Retroviral Vectors Encoding the Human FANCA cDNA Molecular Therapy Vol 5, No 5, May 2002, Part 2 of 2 Parts Copyr[.]
( 2 1 " " 3 > "& β= " 2 3 β= "$*' " T5&H 68: ' 8 = 3 " -TB T8B9 / & ' -/ % 3 2 G # C $ ,998 G ->,8,A/ β= 3 G " " 3 G "%>,8,A C)$(7 β" = &;2D%B ' #.β 7 89&78 0 3 8999 % 1 #) 89978 $ @*' 3 $*' 3 :9 @ "!@ ' #.β ( N" &;2D%B ; 3 @>(4D (7 4 β" = 3 D& -@'* >(/ @*' 3 D, -#!"8/ ? 3 #!"8 @'* >(' ' #.β β" = 3 @'* >( #!"8 #!"8 ' #. #!"8 3 ; # ' #.β )*D4()*7 ' #.β #!"8 3 > #!"8 3 ' #.β *A 1068 Correction of the Hematopoietic Phenotype of Fanconi Anemia A Knockout Mice Using Retroviral Vectors Encoding the Human FANCA cDNA Jose C Segovia,1 Paula Rio,1 Helmut Hennenberg,2 Jose A Casado,1 Jesus Martinez,1 K Göttsche,2 N C Cheng,3 H J Van de Vrugt,3 F Arwert,3 Hans Joenje,3 Juan A Bueren.1 Hematopoiesis, CIEMAT, Madrid, Spain; 2Klinik fŸr Pädiatrische Hämatologie und Onkologie, Z fŸr Kinderheilkunde, HeinrichHeine-Universität, DŸsseldorf, Germany; 3Clinical Genetics and Human Genetics, Free University Medical Center, Amsterdam, Netherlands ? ' -?'/ G > ( 8$! B&H ?' # - ># # + ,EEEI 578:9&/ ?' " * 939 )3) ' 2# " Molecular Therapy Vol 5, No 5, May 2002, Part of Parts Copyright © The American Society of Gene Therapy ' 3 )3) 2# 2# " ) 3) ' 2# " -##/ 8 )3) D"(8"8J 2# )3) 8$! "8/ $*' D @ ! A ' ## )3) 3 )3) G 8$!" )3) )3) )3) ?' 1069 Real-Time PCR SYBR Green Genotype Assay for a Murine Knock-Out Model of Mucopolysaccharidosis Type I Michelle C Rickard,1 Beth E Larson,1 Chester B Whitley.1 Gene Therapy Center - Pediatrics - Institute of Human Genetics, University of Minnesota, Minneapolis, Minnesota, United States -C / G G ( E 3 3 (+2@ - $*'/ !>" 2 # ;;99 1 !@ ! >3 8& ? -0 / 3 B $4' 2 > G - ! A"* " /? " -A)/ * A) ( * -( / 2 G - # ;;99 # / $*' A - ( / !@ ? &9 D 83 (+2@ !@ # #3 -'2/ 89 D $*' =99 # 599 # ? A) &9 D 3 (+2@ !@ # #3 89 D $*' 599 # =99 # ' &9 , 5& 89 69 5& 8& B, 8 (+2@ $*' -* / ? G A)" A) * !@ 0 ? G !@ ? G A) * !@ A) 1# G " !@ (+2@ 3 ) " $*' ( *C !)8"C$=,B&, Molecular Therapy Vol 5, No 5, May 2002, Part of Parts Copyright © The American Society of Gene Therapy 1070 Gene T ransfer into Human Hematopoietic Stem Transfer Cells Application to the Gene Therapy of Congenital Erythropoietic Porphyria Fabien Geronimi,1 Isabelle Lamrissi-Garcia,1 Emmanuel Richard,1 Franỗois Moreau-Gaudry,1 Miquel Morey,2 Hubert de Verneuil.1 Laboratoire PMTG, INSERM EMI 0211, Université Victor Ségalen Bordeaux 2, Bordeaux, France; 2Servicio de Hematologia y Hemoterapia, Hospital Son Dureta, Palma de Mallorca, Spain ->!/ - 4(/ G G ? " % G $=6J >! @ 4( $*' G $=6J 4@)( &=H '88",;H 3 -> ?!/ -D "/ ? 3 C."8" -.(." / >?8α 3 ? 4( 3" >?8α" 4( - >4(/ G " 4 3" >?8α"> ?!"0!@> - >>0/ $=6J -2/ G -!2/ #) #)" ? #) 2 !2 5,H :,H :6H =8H D " 0 $=6J $=6J%=:" !2 3 *)$%($ >! 1071 Highly Efficient Lentiviral V ector-Mediated Vector-Mediated Transduction of Uncultured, Nondividing and Fully ReImplantable Primary Hepatocytes T H Nguyen,1 J Oberholzer,2 J Birraux,3 P Majno,2 D Mattey,2 S Vianin,1 P Morel,2 D Trono.1 Department of Genetics and Microbiology; 2Department of Surgery; 3Department of Pediatrics, University of Geneva Medical school, Geneva, Switzerland ' C C " 3 " " C." 3 C. " " S347 ... ->,8 ,A/ β=